Approved Enzyme Replacement Therapy (ERT) Fabrazyme.
Updated on July 6, 2023.
Approved Enzyme Replacement Therapy (ERT) Elfabrio
Updated on July 6, 2023 .
Approved Enzyme Replacement Therapy (ERT) Replagal in many countries but not in the U.S.
Updated on November 1, 2020.
Candidate AAV gene therapy ST-920 recruiting clinical trial participants.
Updated on July 6, 2023.
Candidate AAV gene therapy 4D-310 recruiting clinical trial participants.
Updated on July 6, 2023.
Gene therapy offers the prospect of long-term and potentially curative benefits to patients with genetic or acquired diseases ....
Updated on November 22, 2020.